enzyme replacement therapy
Showing 1 - 25 of >10,000
Gaucher Disease Type 1 Trial in Jerusalem (Enzyme replacement therapy for Gaucher disease in combination with altus care
Completed
- Gaucher Disease Type 1
- Enzyme replacement therapy for Gaucher disease in combination with altus care application
-
Jerusalem, IsraelHebrew university
Sep 18, 2023
Sphingomyelin Lipidosis Trial (olipudase alfa (GZ402665))
Approved for marketing
- Sphingomyelin Lipidosis
- olipudase alfa (GZ402665)
- (no location specified)
Sep 15, 2022
Gaucher Disease, Type 3 Trial (Gene therapy, Enzyme Replacement Agent)
Not yet recruiting
- Gaucher Disease, Type 3
- Gene therapy
- Enzyme Replacement Agent
- (no location specified)
Apr 14, 2023
Acute Pancreatitis, Exocrine Pancreatic Insufficiency, Gut Microbiota Trial in Coimbra (Pancreatic Enzyme Replacement Therapy,
Recruiting
- Acute Pancreatitis
- +3 more
- Pancreatic Enzyme Replacement Therapy
- Placebo
-
Coimbra, PortugalCentro Hospitalar e Universitário de Coimbra, E.P.E.
Jul 27, 2022
Pancreatic Exocrine Insufficiency, Pancreatic Enzyme Replacement Therapy, Pancreaticoduodenectomy Trial in Shanghai (Pancreatin
Recruiting
- Pancreatic Exocrine Insufficiency
- +2 more
- Pancreatin Enteric-coated Capsules
- Routine treatment plan
-
Shanghai, Shanghai, ChinaShanghai Ruijin Hospital
Nov 1, 2023
Gaucher Disease, Type 1 Trial in Jerusalem (Ambroxol)
Active, not recruiting
- Gaucher Disease, Type 1
-
Jerusalem, IsraelShaare Zedek Medical Center
May 24, 2022
ERT in Pompe Disease: Elucidation of Molecular Structures
Not yet recruiting
- Pompe-Disease
-
Rüsselsheim, Hessen, GermanyCentre for Analytical Biochemistry
Jan 30, 2023
Fabry Disease Trial in Taipei
Recruiting
- Fabry Disease
-
Taipei, TaiwanInvestigational Site Number :1580001
Sep 24, 2023
MPS II Immunophenotyping
Recruiting
- MPS II
- +2 more
-
Durham, North CarolinaDuke University
Jun 3, 2022
MPS I, MPS II, MPS IVA Trial in San Francisco (Aldurazyme (laronidase))
Recruiting
- MPS I
- +8 more
- Aldurazyme (laronidase)
-
San Francisco, CaliforniaUniversity of California
Apr 21, 2022
Both Patients and Their Clinicians in Treatment of Fabry Disease
Completed
- Fabry Disease
- Agalsidase Beta
- Agalsidase Alpha
-
Philadelphia, Pennsylvania
- +8 more
Oct 27, 2022
Unresectable Pancreatic Cancer Trial (creon 35.000 Ph.U (R), Best Standarard of Care)
Not yet recruiting
- Unresectable Pancreatic Cancer
- creon 35.000 Ph.U (R)
- Best Standarard of Care
- (no location specified)
Oct 19, 2023
Mucopolysaccharidosis I Trial in Wuhan (Laronidase)
Recruiting
- Mucopolysaccharidosis I
-
Wuhan, ChinaInvestigational Site Number :1560001
Jan 15, 2023
Mucopolysaccharidosis Trial in Gaziantep (Enzyme Replacement Agent)
Completed
- Mucopolysaccharidosis
- Enzyme Replacement Agent
-
Gaziantep, None Selected, TurkeySerkan Usgu
Aug 7, 2021
Velaglucerase Alfa Given as Standard Patient Care in Young
Recruiting
- Gaucher Disease
- Standard of Care
-
Fairfax, VirginiaLysosomal & Rare Disorders Research & Treatment Center
Jan 5, 2023
Pompe Disease (Late-onset) Trial in Durham (Clenbuterol, Placebos)
Withdrawn
- Pompe Disease (Late-onset)
- Clenbuterol
- Placebos
-
Durham, North CarolinaDuke University Medical Center
Aug 15, 2022
Patients With Juvenile-onset Pompe Disease
Recruiting
- Pompe's Disease Juvenile Onset
-
Nancy, FranceChildren's Hospital - CHRU de Nancy
Jul 2, 2021
Metastatic Pancreatic Ductal Adenocarcinoma, Metastatic Pancreatic Cancer, Metastatic Pancreatic Adenocarcinoma Trial in New
Recruiting
- Metastatic Pancreatic Ductal Adenocarcinoma
- +12 more
-
New York, New YorkMemorial Sloan Kettering Cancer Center
Nov 30, 2022
Fabry's Disease Trial in China (Agalsidase beta)
Active, not recruiting
- Fabry's Disease
- Agalsidase beta
-
Beijing, China
- +5 more
May 4, 2022
Pancreatic Adenocarcinoma Trial in Los Angeles (Pancrelipase)
Recruiting
- Pancreatic Adenocarcinoma
-
Los Angeles, CaliforniaCedars-Sinai Medical Center
Jul 15, 2022
Pancreatic Insufficiency Trial in Canada (PERT at discharge, Standard of Care)
Not yet recruiting
- Pancreatic Insufficiency
- PERT at discharge
- Standard of Care
-
Hamilton, Ontario, Canada
- +5 more
Jul 18, 2022
Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal
Recruiting
- Fabry Disease
-
Minneapolis, Minnesota
- +1 more
Sep 16, 2022
Mucopolysaccharidosis II Trial in Worldwide (Iduronate-2-sulfatase enzyme replacement therapy, iduronate-2-sulfatase enzyme
Completed
- Mucopolysaccharidosis II
- Iduronate-2-sulfatase enzyme replacement therapy
- +2 more
-
Oakland, California
- +8 more
May 30, 2021
Gaucher Disease Trial in Hamamatsu, Minato-ku, Osaka (velaglucerase alfa)
Completed
- Gaucher Disease
- velaglucerase alfa
-
Hamamatsu, Shizuoka, Japan
- +2 more
Jun 25, 2021